• Study Resource
  • Explore Categories
    • Arts & Humanities
    • Business
    • Engineering & Technology
    • Foreign Language
    • History
    • Math
    • Science
    • Social Science

    Top subcategories

    • Advanced Math
    • Algebra
    • Basic Math
    • Calculus
    • Geometry
    • Linear Algebra
    • Pre-Algebra
    • Pre-Calculus
    • Statistics And Probability
    • Trigonometry
    • other →

    Top subcategories

    • Astronomy
    • Astrophysics
    • Biology
    • Chemistry
    • Earth Science
    • Environmental Science
    • Health Science
    • Physics
    • other →

    Top subcategories

    • Anthropology
    • Law
    • Political Science
    • Psychology
    • Sociology
    • other →

    Top subcategories

    • Accounting
    • Economics
    • Finance
    • Management
    • other →

    Top subcategories

    • Aerospace Engineering
    • Bioengineering
    • Chemical Engineering
    • Civil Engineering
    • Computer Science
    • Electrical Engineering
    • Industrial Engineering
    • Mechanical Engineering
    • Web Design
    • other →

    Top subcategories

    • Architecture
    • Communications
    • English
    • Gender Studies
    • Music
    • Performing Arts
    • Philosophy
    • Religious Studies
    • Writing
    • other →

    Top subcategories

    • Ancient History
    • European History
    • US History
    • World History
    • other →

    Top subcategories

    • Croatian
    • Czech
    • Finnish
    • Greek
    • Hindi
    • Japanese
    • Korean
    • Persian
    • Swedish
    • Turkish
    • other →
 
Profile Documents Logout
Upload
Gene therapy: Current status and future perspectives
Gene therapy: Current status and future perspectives

... The first successful gene therapy trial was performed on a 4 year old girl named Ashanti Desilva, with a rare genetic immune system disorder called severe combined immune deficiency (SCID) on 14 September 1990 at the National Institute of Health, under the direction of professor William French Ander ...
cystic fibrosis pedigree
cystic fibrosis pedigree

... Cystic fibrosis is a genetic disorder. Individuals with CF have an excess amount of fluid produced in their lungs, leading to severe respiratory problems. People with CF often die within their first year of life. The gene for CF is not found on the sex chromosomes. Therefore, males and females will ...
DRS35432-LCx-221 (5/12) - North Carolina General Assembly
DRS35432-LCx-221 (5/12) - North Carolina General Assembly

... patterns in patients' cancers, allowing doctors to accurately predict response to therapy and to select individualized treatment. The multiple gene mutations that cause each cancer produce subtle changes in expression of the 35,000 genes encoded in our DNA. Bioinformatics algorithms will catalog the ...
The Human Genome Project: An Insight to the Homo Sapiens
The Human Genome Project: An Insight to the Homo Sapiens

... Since He is Witness over all things?" Al-Qur'an, Surah Fusilat, 41: 53 One of these tools is genetic mapping. Genetic mapping also called linkage mapping - can offer firm evidence that a disease transmitted from parent to child is linked to one or more genes. Mapping also provides clues about which ...
Osteogenesis Imperfecta
Osteogenesis Imperfecta

cloning
cloning

... (b) It is this portion of the genome which is removed and cloned DNA inserted (3) Genes for host cell lysis are encoded on the right portion of the genome c) Cloning procedure (1) Digest with restriction enzymes (a) This will create sticky ends and separate the left and right arms from the middle DN ...
Hardy-Weinberg Practice Problems
Hardy-Weinberg Practice Problems

... q = allele frequency of recessive traits ...
Diapositive 1 - Moodle Lille 2
Diapositive 1 - Moodle Lille 2

Dihybrid crosses and gene linkage
Dihybrid crosses and gene linkage

... A new shuffling of the alleles has created a new combination which does not match either of the parents’ genotypes The term recombinant is used to describe both the new chromosome and the resulting organism. Recombinants form through the process of crossing over ...
Heredity Power Point - Auburn School District
Heredity Power Point - Auburn School District

... F. What countries have the most people that are color blind? G. Is there a cure for color blindness? Can it be prevented? ...
SUMMARY NOTIFICATION INFORMATION FORMAT FOR THE RELEASE OF GENETICALLY MODIFIED HIGHER PLANTS
SUMMARY NOTIFICATION INFORMATION FORMAT FOR THE RELEASE OF GENETICALLY MODIFIED HIGHER PLANTS

... involved in the host-pathogen interaction, the expression of the NB-LRR genes can occur at the earlier or later stages of the infection process. The effect of the cisgene in S. tuberosum cv. Desiree is that it will display strong resistance to P. infestans, in contrast to the highly P. infestans sus ...
GENES IN ACTION Section 1: Mutation and Genetic Change Key
GENES IN ACTION Section 1: Mutation and Genetic Change Key

... Note that although cancers result from somatic cell mutations, not all somatic cell mutations cause cancer. New Alleles For a given gene, many alleles, or variations, may exist. Any new allele must begin as a mutation of an existing allele. Most new alleles are simply the result of silent mutations, ...
Multimedia Information Gathering
Multimedia Information Gathering

... I(X,Y)=H(X)-H(X|Y)= H(Y)-H(Y|X) Ranking based on mutual information  H ( X )  H (Y )  H ( X , Y )  U ( X , Y )  2 ...
System approaches for complex diseases
System approaches for complex diseases

... Wt Gain in DIO C57BL/6 Mice ...
manuka short course
manuka short course

... An Introduction to Nutrigenetics & Nutrigenomics will define and illustrate (with practical examples) the difference between nutrigenetics, nutrigenomics and epigenetics. In this module we will also explore the concept of food responsiveness including examples illustrating how they can be used in cl ...
Genetics And Huntington Disease
Genetics And Huntington Disease

... • NIPT Non invasive prenatal screening/testing • Blood test during first trimester of pregnancy • Measure CAG repeats • Confirm with diagnostic test ...
Honors Biology - ahs-guntherbiology-2009
Honors Biology - ahs-guntherbiology-2009

... __________ 12. In Laborador retrievers, coat color is controlled by two genes. Black coat color (B) is dominat to brown coat color (b). However, dogs that are homozygous recessive at another unlinked gene (e) are yellow. A dog that has genotype EdBb (black) is bred with another dog whose genotype is ...
LIBACS_Hull_Volpato - Faculty of Medicine and Health
LIBACS_Hull_Volpato - Faculty of Medicine and Health

Document
Document

... You have 2 hours to complete this exam, which is worth 30 percent of your grade. There are 6 questions, worth 6 points each. I will take your best 5 answers, so you only need to answer 5 of the 6 questions. Each question has two short-answer parts that generally have answers that can be found in the ...
Albinism Powerpoint
Albinism Powerpoint

...  Causes eyes to appear pink as well as ...
PDF - European Journal of Biotechnology and Bioscience
PDF - European Journal of Biotechnology and Bioscience

... predicted to be the primary cause of the long term gene expression. In contrast to adenoviruses, most people treated with AAV will not build an immune response to remove the virus and the cells that have been successfully treated with it. Several trials with AAV are on-going or in preparation, mainl ...
genetics - MrsGorukhomework
genetics - MrsGorukhomework

... **Drosophila (fruit fly) shows linked genes. Morgan found that when crossing, didn’t get expected ratio. First was a pure breeding tan body with long wings crossed with black body ad short wings (vestigial wings). F1 all had tan bodies and long wings but the F2 was 75% tan, long wings and 25% black ...
Adult Acute Myeloid Leukemia
Adult Acute Myeloid Leukemia

... (a donor) whose tissue is the same or almost the same as that of the patient. The donor may be a twin (the best match), a brother or sister, or a person who is not related. The healthy stem cells from the donor are then transferred to the patient through a needle in the vein, and the new marrow repl ...
Gene Mutations
Gene Mutations

14 – Mendel and the Gene Idea
14 – Mendel and the Gene Idea

... - Diagram that shows how traits are passed over generations Circles = females Squares = males Individual with trait = filled in CARRIER = half/half filled in KARYOTYPE - organizes picture of an individual’s chromosomes Can show sex: XX = female / XY = male Can show some genetic disorders: *missing/e ...
< 1 ... 365 366 367 368 369 370 371 372 373 ... 556 >

Gene therapy



Gene therapy is the therapeutic delivery of nucleic acid polymers into a patient's cells as a drug to treat disease. Gene therapy could be a way to fix a genetic problem at its source. The polymers are either expressed as proteins, interfere with protein expression, or possibly correct genetic mutations.The most common form uses DNA that encodes a functional, therapeutic gene to replace a mutated gene. The polymer molecule is packaged within a ""vector"", which carries the molecule inside cells.Gene therapy was conceptualized in 1972, by authors who urged caution before commencing human gene therapy studies. By the late 1980s the technology had already been extensively used on animals, and the first genetic modification of a living human occurred on a trial basis in May 1989 , and the first gene therapy experiment approved by the US Food and Drug Administration (FDA) occurred on September 14, 1990, when Ashanti DeSilva was treated for ADA-SCID. By January 2014, some 2,000 clinical trials had been conducted or approved.Early clinical failures led to dismissals of gene therapy. Clinical successes since 2006 regained researchers' attention, although as of 2014, it was still largely an experimental technique. These include treatment of retinal disease Leber's congenital amaurosis, X-linked SCID, ADA-SCID, adrenoleukodystrophy, chronic lymphocytic leukemia (CLL), acute lymphocytic leukemia (ALL), multiple myeloma, haemophilia and Parkinson's disease. Between 2013 and April 2014, US companies invested over $600 million in the field.The first commercial gene therapy, Gendicine, was approved in China in 2003 for the treatment of certain cancers. In 2011 Neovasculgen was registered in Russia as the first-in-class gene-therapy drug for treatment of peripheral artery disease, including critical limb ischemia.In 2012 Glybera, a treatment for a rare inherited disorder, became the first treatment to be approved for clinical use in either Europe or the United States after its endorsement by the European Commission.
  • studyres.com © 2026
  • DMCA
  • Privacy
  • Terms
  • Report